Medscape
The only approved ocular gene therapy, which targets a specific gene mutation in two forms of inherited retinal disease, has shown evidence in a real-world study from the United Kingdom that young children derive a greater improvement in vision than adults who undergo the procedure. The study included 14 eyes in eight patients with two …
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In Gene Therapy for RP, LCA, the Earlier, the Better
The only approved ocular gene therapy, which targets a specific gene mutation in two forms of inherited retinal disease, has shown evidence in a real-world study from the United Kingdom that young children derive a greater improvement in vision than adults who undergo the procedure. The study included 14 eyes in eight patients with two